This is the first successful treatment to slow the progression of Huntington's disease after decades of failed attempts. The 75% reduction in disease advancement means patients can maintain independence and quality of life for years longer than previously possible. One patient even returned to work after undergoing medical retirement, proving that this therapy delivers real-world benefits beyond clinical measurements.
While promising, this expensive treatment requiring complex 18-hour brain surgery will remain inaccessible to most patients who desperately need it. The results are based on only 29 patients without peer review, and the therapy doesn't cure the disease but merely delays the inevitable, gradual decline. Gene therapies often carry hefty price tags that healthcare systems struggle to afford, further exacerbating inequalities in access to care.
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